Proposal to sustain the clinical and research activity of the children’s Neuromuscular (NM) service in Leeds, whilst securing engagement of the service with national initiatives to promote best possible patient care

A2003206

The Leeds Children’s Neuromuscular service, a national centre of excellence for Duchenne Muscular Dystrophy (DMD) and Spinal Muscular Atrophy (SMA), this investment will be used to expand clinical and research capacity. This includes dedicated consultant time and a Clinical Trials Coordinator to support complex clinical trials, including advanced gene therapy studies. The investment strengthens Leeds’ leadership in Neuromuscular research, enhances patient care, and increases trial recruitment. Duchenne UK has partnered in this initiative, matching the funding to support ongoing advancements. These roles will enable increased trial activity, improved patient experiences, and important research outputs.

Lead Researcher

Dr Anne-Marie Childs
Consultant Paediatric Neurologist

Host Organisation

Leeds Teaching Hospitals NHS Trust

Grant Amount £154,726.00
Start Date 01/04/2025
Estimated Duration 48 months
Impact Areas Treatment of Rare Conditions
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